July 27, 2026

What to Know Ahead of This Week’s Deramiocel FDA Advisory Committee Meeting

On Wednesday, July 29, 2026, the FDA’s Cellular, Tissue, and Gene Therapies Advisory Committee (CTGTAC) will meet to review Capricor Therapeutics’ Biologics License Application (BLA) for Deramiocel as a potential treatment for Duchenne. The meeting…

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July 10, 2026

Highlights from PPMD’s 2026 Annual Conference

Whether you joined us in Orlando or are catching up from home, the learning opportunities from PPMD’s 2026 Annual Conference continue. We’re excited to share that recordings and resources from PPMD’s 2026 Annual Conference are…

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June 27, 2026

Catching Up on PPMD’s 2026 Annual Conference: Part II

PPMD’s 2026 Annual Conference brought together individuals and families from across the Duchenne and Becker community for three days filled with scientific presentations, discussions around care, clinical trials and quality of life, and of course,…

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June 26, 2026

Catching up on What’s Happening at PPMD’S 2026 Annual Conference

PPMD’s 2026 Annual Conference is in full swing! PPMD’s 2026 Annual Conference kicked off with opening remarks from Katherine Beaverson, MD, CEO of PPMD, who welcomed attendees, introduced the dedicated PPMD team, recognized the many…

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May 15, 2026

NEW: Livestream with the PAAC

What can you learn from the PPMD Adult Advisory Committee (PAAC) that you can’t ask Google? Honestly? A lot. Google can give you information, but it can’t tell you what it’s actually like to live with…

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April 30, 2026

Catch up on PPMD Together: Philadelphia

This past weekend, PPMD kicked off our 2026 PPMD Together series in Philadelphia, Pennsylvania. Individuals with Duchenne and Becker, their families, clinicians, and industry partners gathered for a day and a half full of connection…

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November 27, 2025

A Thanksgiving Message from Pat

This Thanksgiving, I find myself reflecting deeply on gratitude, especially for this incredible community that feels like family. This season always brings a moment to pause, to take stock of where we’ve been and where…

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November 20, 2025

Closing Out the Year with Connection & Community at PPMD Together

Recently, the Duchenne and Becker community gathered virtually for the final PPMD Together meeting of the year. This intimate session centered on fostering friendships for everyone in the family while living with dystrophinopathy.  The meeting,…

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November 14, 2025

PPMD Continues to Drive Progress with Your Support

PPMD is committed to every future, working toward the day when every single family has options for, and access to, therapies and specialized care. In 2025, thanks to your support, families are receiving earlier diagnoses,…

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November 10, 2025

Tips for Smooth Holiday Travel

The holidays are a special time to connect with family and friends, and for many, that involves travel. To help make your journey a little easier, PPMD has gathered some helpful travel tips and resources!…

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