Poster
PPMD Certified Duchenne Care Center (CDCC): Research Designation
Care
CDCC, Clinical Care, Duchenne, Research
Poster
DMD testing in males unknown to have a dystrophinopathy – A retrospective analysis from a sponsored DMD testing program
Genetics
Expanded carrier screening, Genetic Counseling, Genetics
Abstract
Molecular insights and cautionary tale of Duplications in Duchenne and Becker Muscular Dystrophy Across a Large Cohort.
Genetics
Expanded carrier screening, Genetic Counseling, Genetics
Journal
Motor function and growth outcomes with early corticosteroid initiation in DMD: an adjusted cross-trial comparison
Care
Ambulation, Clinical Care, Corticosteroids, Duchenne
Journal
Incremental Disease Burden (Healthcare Costs and Resources) of Duchenne Muscular Dystrophy in the US: A Matched Cohort Analysis
Care
Treatment access
Journal
Meeting Report: Translating exercise research in dystrophinopathy to the clinic
Care
Care, Exercise, Physical Therapy
Journal
Adrenal Suppression in Duchenne Muscular Dystrophy: Management Strategies Incorporating Novel Steroid Vamorolone
Care
Care, Endocrinology, Steroids
Journal
Healthcare providers’ practices and perspectives on discussing life expectancy with patients with Duchenne muscular dystrophy and their caregivers
Care
Care, Quality of Life
Journal
Meeting Report: Expanding Access to Advanced Cardiac Therapies, Including Ventricular Assist Devices (VADs) and Heart Transplantation in Muscular Dystrophy
Care
Cardiac
Journal
Functional and structural pathologies in skeletal muscle of a rat model of Duchenne muscular dystrophy
Basic Science
Animal model, basic science