September 22, 2023

Miles for Matthew Celebrates 15 Years

For 15 years, residents of Greensboro, North Carolina have supported PPMD’s mission by participating in Miles for Matthew. Created and organized by the Greiner family, in honor of their son Matthew, this 5K and 10K…

Learn More

September 21, 2023

CDCC Spotlight: Children’s Hospital Los Angeles

Breaking Barriers: Dedication to All Families Dr. Leigh Ramos-Platt, MD, Medical Director of the Children’s Hospital Los Angeles’ (CHLA) Certified Duchenne Care Center in the hospital’s Neurological Institute, dedicates her career to serving young patients…

Learn More

September 21, 2023

Entrada Therapeutics starts dosing in ENTR-601-44 Phase 1 trial

Entrada Therapeutics has announced that the first participant has been dosed in its Phase 1 clinical trial evaluating ENTR-601-44, the company’s proprietary Endosomal Escape Vehicle (EEV™)-conjugated phosphorodiamidate morpholino oligomer (PMO), for the potential treatment of…

Learn More

September 19, 2023

RSV, COVID, and Flu – oh my!

As school has started and the winter season approaches, the increase in respiratory viruses is soon to come. This year it’s important to protect yourself, your children and your family from all respiratory viruses, but…

Learn More

September 15, 2023

PTC Therapeutics Announces Negative European Medicines Agency Opinion Regarding Full Authorization of Translarna

PTC Therapeutics today shared that the Committee for Medicinal Products for Human Use (CHMP) of the European Medicines Agency (EMA) has recommended not renewing the Marketing Authorization for Translarna™ (ataluren), a treatment for Duchenne patients…

Learn More

September 13, 2023

Game Day Tips for Coach to Cure MD 2023

The 16th Annual Coach to Cure MD Game Day is Saturday, September 30th! With over 280 schools participating this year, we couldn’t be more grateful to have you on our team! There will be plenty…

Learn More

September 11, 2023

Duchenne Action Month: Ways to get involved with PPMD

We know that no one person, company, or organization will end Duchenne. That’s why we are grateful to all of our collaborators – individuals, organizations, and industry partners – who, by joining forces with PPMD,…

Learn More

August 31, 2023

CDCC Spotlight: Arkansas Children’s Hospital

Reaching Rural Areas When thinking of expert Duchenne care and research, one may think it only exists in large cities. However, Dr. Aravindhan Veerapandiyan, aka Dr. Panda, the Director of Arkansas Children’s Certified Duchenne Care…

Learn More

August 30, 2023

FibroGen Announces Topline Data from Phase 3 LELANTOS-2 Study

FibroGen has announced topline results of the Phase 3 LELANTOS-2 trial of pamrevlumab, their investigational anti-fibrotic monoclonal antibody, for ambulatory patients with Duchenne muscular dystrophy.  Although generally safe and well tolerated, pamrevlumab did not meet…

Learn More

August 29, 2023

Breaking barriers together, this Duchenne Action Month and every day

On September 7, we will once again join forces with Duchenne and Becker organizations, families, partners, and all those like minded individuals around the globe to commemorate World Duchenne Awareness Day. This year we acknowledge…

Learn More