Blog

Physical Therapy for Your Lungs

The lungs of people living with Duchenne are not directly affected by the lack of dystrophin in Duchenne. However, the muscles responsible for breathing, including the diaphragm and the intercostal muscles (the tiny muscles between…

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Solid Biosciences Shares Letter to the Duchenne Community: COVID-19 Update

Solid Biosciences Inc. has shared an update with the community regarding the IGNITE DMD clinical hold and COVID-19. Solid’s Letter to the Duchenne Community: Letter to the Duchenne Community: COVID-19 Update Dear Duchenne Community, During…

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Pfizer Shares Update on PF-06939926 Gene Therapy Trial and COVID-19

Pfizer has shared an update regarding the PF-06939926 gene therapy trial and COVID-19. Read Pfizer’s update: Our Clinical Trials UPDATE: March 25 —To avoid adding to the demands on the healthcare system during this unprecedented…

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WATCH: COVID-19 & Medications – What is safe in Duchenne?

Webinar Recording: COVID-19 & Medications — What is Safe in Duchenne? On March 26, PPMD hosted a webinar: COVID-19 & Medications: What is Safe in Duchenne? We were joined by four Duchenne specialists from our…

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Italfarmaco Shares Community Update on Givinostat Trials & COVID-19

Italfarmaco has shared an update with the community regarding givinostat clinical trials and COVID-19. Read the update from Italfarmaco Dear Duchenne Community, ITALFARMACO team would like to take this opportunity to inform you that we…

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PTC Shares Additional Update on the Availability of EMFLAZA During COVID-19

PTC has provided additional details about Emflaza during the COVID-19 pandemic. Read PTC Therapeutic’s Statement PTC Therapeutics, Inc. Update on the Availability of EMFLAZA March 27, 2020 We want to assure patients and health care…

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Catabasis Shares March 2020 Newsletter

Catabasis Pharmaceuticals has shared the latest edition of their community newsletter, including information about edasalonexent and COVID-19, and responses to questions they have received. Click here to download the PDF.

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Gratitude

All of us are more than a little panicked about COVID-19. This is such an uncertain time and these frightening feelings can be contagious as well. But so are feelings of kindness, positivity, gratitude, and…

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NS Pharma Announces Marketing Authorization in Japan of VILTEPSO® for the Treatment of Duchenne

Good news out of Japan! NS Pharma, Inc., announced that their parent company, Nippon Shinyaku Co., Ltd., has received approval for viltolarsen in Japan for people with Duchenne amenable to exon 53 skipping therapy. Viltolarsen…

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WATCH: Family Friday – Home Schedules & School

Webinar Recording: Family Friday – Home Schedules & School For many of us, self-quarantine is in full swing, and adjusting to a different family structure may be overwhelming. So your PPMD family is launching Family…

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