March 28, 2018

End Duchenne Tour Recap: Grand Rapids, MI

PPMD was excited to head to the Midwest for the second stop on the 2018 End Duchenne Tour. The event took place at Western Michigan University in Grand Rapids, Michigan, in partnership with Team Joseph, Little…

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March 27, 2018

Center Directors Publish Collective Statement Regarding Patient Access to Approved Therapies

PPMD is proud to announce the publication of a collective statement regarding patient access to approved therapies from the center directors of our Certified Duchenne Care Centers. There are many ongoing treatment trials for Duchenne and…

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March 26, 2018

[WEBINAR] What is a Master Protocol?

PPMD fights to end Duchenne for every single family. As part of our mission, we believe that we must continually work to identify and explore innovative opportunities that may accelerate the drug development and clinical…

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March 21, 2018

Race Athlete Spotlight: Emma & Alexis Broggi

Meet Emma Broggi, 17 years old and Alexis Broggi, 14 years old: Why did you choose to join the Race to End Duchenne team? Soon after we met Danny and his family, our family chose…

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March 13, 2018

Duchenne Pulmonary Awareness Video Series

Pulmonary management in Duchenne (all of the care involved with breathing and coughing) can be confusing and difficult to understand. There are many terms, abbreviations, and procedures that all sound very complicated. PPMD – with support from…

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March 8, 2018

PPMD’s Historic Compass Meeting

There are hardly words to capture the impact our unified community had on Monday. We had traveled from all over the nation to convene with federal policymakers, industry partners, and payers for the Duchenne Patient-Focused Compass…

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February 15, 2018

FDA Publishes Finalized Duchenne Guidance for Drug Development

Today is a historic moment for the Duchenne community, as moments ago the FDA published the finalized “Duchenne Muscular Dystrophy and Related Dystrophinopathies: Developing Drugs for Treatment” Guidance for Industry (click here to access), along with four other guidances….

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February 15, 2018

End Duchenne Tour Recap: Morristown, NJ

PPMD kicked off the 2018 End Duchenne Tour with a stop in our very own backyard – Goryeb Children’s Hospital in Morristown, New Jersey! PPMD was extremely grateful to partner with Michael’s Cause, Pietro’s Fight, Powers Promise,…

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February 7, 2018

From Our Hearts to Yours — Updates in Duchenne Cardiac Care Guidelines

Care for the heart has long been a priority for PPMD. Over the past several years, PPMD’s Cardiac Initiative has given rise to: A meeting convened in partnership with the National Heart Lung and Blood Institute that…

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February 2, 2018

#KOMD fights to End Duchenne

The Curran family received their son’s diagnosis on April 21, 2015. They were at a loss and felt alone and overwhelmed, but luckily they have the greatest support system they could have ever asked for….

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