March 28, 2022

NIH Hosts Working Group to Better Understand Immune Response in Gene Therapy Trials (Webinar Recording)

Gene therapy, as we have often discussed, is still in its early days; meaning there are lots of lessons to be learned and new challenges that arise to ensuring all patients can one day have…

Learn More

March 17, 2022

PPMD Convenes 80+ Expert Cardiologists & Professionals for Duchenne Cardiac Care Meeting

PPMD is spending this week joined by 80+ expert cardiologists, key neuromuscular providers, members of the FDA and NIH, and industry partners to discuss cardiac care in Duchenne. We all know that the heart is…

Learn More

February 3, 2022

New Study to Understand Duchenne Patients’ and Caregivers’ Attitudes Towards Gene Therapy Launched

In a new transatlantic collaboration, Parent Project Muscular Dystrophy (PPMD) and Duchenne UK (DUK), the DMD Hub, and RTI International are conducting a study to explore attitudes towards gene therapy and gene editing from adults…

Learn More

January 26, 2022

Save the Date for PPMD’s Upcoming Events!

PPMD is excited to announce our 2022 schedule of educational events, including PPMD’s Annual Conference (hybrid in-person & virtual meeting), End Duchenne Tour (both in-person and virtual stops), and Advocacy Conference (virtual). New this year, PPMD will host The Power of…

Learn More

January 4, 2022

Thank YOU for Joining the Power of Us!

I am grateful for your generosity this year and excited to announce that we have reached our goal of providing supplemental funding to the Wellstone Muscular Dystrophy Cooperative Research Centers. The Power of Us is…

Learn More

December 30, 2021

Tomorrow is the last chance to double your gift

I can’t believe it’s almost the beginning of a new year. In about a week, I will lace up my sneakers once again and join my chosen family for another Walt Disney World Marathon Weekend….

Learn More

December 26, 2021

Double the Impact of Your Gift Today!

Once Duchenne enters your life, you learn to be resilient even if it is against your wishes. You learn to come together to get through the tough times, even if it is with a community…

Learn More

December 17, 2021

Gene Editing Therapy Start-up Secures $3.4 Million Grant for Duchenne Research

MyoGene Bio has received a $3.4 million grant from the California Institute of Regenerative Medicine to advance its pre-clinical gene-editing studies in Duchenne, thanks to support from Parent Project Muscular Dystrophy (PPMD), Duchenne UK, and…

Learn More

December 15, 2021

Help PPMD raise $400,000 to invest in the future of Duchenne research

I am humbled to be working in Duchenne research, where patients and families have been the relentless driving force behind the progress we’ve made so far. We have seen the Power of Us realized, as…

Learn More

December 15, 2021

Second Chance — Win a NEW Nintendo Switch OLED!

THANK YOU, Duchenne Registry participants! As you might have heard, The Duchenne Registry was thrilled to recently give away a Nintendo Switch OLED to a Duchenne Registry participant who completed all of their surveys. The…

Learn More