Gene Therapy Approaches to Replace or Restore Dystrophin PF-06939926 – Kasia Lobello, MD (Pfizer, Inc.) RGX-202 – Jahannaz Dastgir, DO (REGENXBIO) scAAV9.U7-ACCA – Kevin Flanigan, MD (Nationwide Children’s Hospital) SGT-001 – Carl Morris, PhD (Solid Biosciences) SRP-9001 – Teji Singh, MD (Sarepta Therapeutics) 3 years ago 2022 PPMD Annual Conference,Conferences & Meetings You may also like 44:59 CINRG Expanded Duchenne Natural History Study (eDNHS) 6 years ago Conferences & Meetings,Foundations of Drug Development 37:11 Genetics & The Duchenne Registry 6 years ago Beginning the Duchenne Journey,Conferences & Meetings 24:30 Research & Clinical Trials 6 years ago Beginning the Duchenne Journey,Conferences & Meetings 4:10 PPMD Community: Getting Involved 6 years ago Beginning the Duchenne Journey,Conferences & Meetings 22:23 Advocacy & Community Engagement 6 years ago Beginning the Duchenne Journey,Conferences & Meetings 22:23 Navigating the Challenges of School 6 years ago Beginning the Duchenne Journey,Conferences & Meetings 24:00 Physical Therapy 6 years ago Beginning the Duchenne Journey,Conferences & Meetings 19:53 Establishing a Care Plan 6 years ago Beginning the Duchenne Journey,Conferences & Meetings «1…1819202122…28»Page 20 of 28