Gene Therapy Approaches to Replace or Restore Dystrophin PF-06939926 – Kasia Lobello, MD (Pfizer, Inc.) RGX-202 – Jahannaz Dastgir, DO (REGENXBIO) scAAV9.U7-ACCA – Kevin Flanigan, MD (Nationwide Children’s Hospital) SGT-001 – Carl Morris, PhD (Solid Biosciences) SRP-9001 – Teji Singh, MD (Sarepta Therapeutics) 3 years ago 2022 PPMD Annual Conference,Conferences & Meetings You may also like 37:30 In the Pipeline: Combating Fibrosis and Inflammation 5 years ago 2020 PPMD Virtual Conference: Live Sessions,Conferences & Meetings 45:13 Duchenne Care: The Role of Physical Medicine & Rehabilitation (PM&R) in Neuromuscular Care 5 years ago 2020 PPMD Virtual Conference: Live Sessions,Conferences & Meetings 17:25 Cannabis & Duchenne 5 years ago 2020 PPMD Virtual Conference: Live Sessions,Conferences & Meetings 1:04:27 Rescuing the Heart: Why Cardiac Intervention Is So Critical 5 years ago 2020 PPMD Virtual Conference: Live Sessions,Conferences & Meetings 31:39 Emerging Strategies in Duchenne 5 years ago 2020 PPMD Virtual Conference: Live Sessions,Conferences & Meetings 14:12 Closing Address: Looking Ahead to 2021 5 years ago 2020 PPMD Virtual Conference: Live Sessions,Conferences & Meetings 26:14 Imaging DMD 6 years ago Conferences & Meetings,Resources & Tools 45:00 Gene Therapy: Q&A 6 years ago Conferences & Meetings,In the Pipeline: Gene Therapy gene therapy «1…1718192021…28»Page 19 of 28