Gene Therapy Approaches to Replace or Restore Dystrophin PF-06939926 – Kasia Lobello, MD (Pfizer, Inc.) RGX-202 – Jahannaz Dastgir, DO (REGENXBIO) scAAV9.U7-ACCA – Kevin Flanigan, MD (Nationwide Children’s Hospital) SGT-001 – Carl Morris, PhD (Solid Biosciences) SRP-9001 – Teji Singh, MD (Sarepta Therapeutics) 2022 PPMD Annual Conference,Conferences & Meetings 3 years ago You may also like 17:38 About PPMD: Our Story 5 years ago Beginning the Duchenne Journey,Conferences & Meetings 1:02:07 Teen & Adult Track – Intro to the Teen & Adult Track (PAAC) 5 years ago Conferences & Meetings,For Teens & Adults,Teen & Adult Track 52:33 Muscle Physiology and Exercise in Duchenne 5 years ago Conferences & Meetings,Resources & Tools 1:27 Kinova Robotics 5 years ago Conferences & Meetings,Resources & Tools 1:00 Nationwide Children’s Hospital 5 years ago Conferences & Meetings,Resources & Tools 0:52 Jett Foundation 5 years ago Conferences & Meetings,Resources & Tools 2:39 Restoration of Arm Mobility with Power-Assist Exoskeletons 5 years ago Conferences & Meetings,Resources & Tools 17:08 Tech Life Hacks for Adults with Duchenne 5 years ago Conferences & Meetings,For Teens & Adults,Teen & Adult Track «1…1920212223…28»Page 21 of 28