Gene Therapy Approaches to Replace or Restore Dystrophin PF-06939926 – Kasia Lobello, MD (Pfizer, Inc.) RGX-202 – Jahannaz Dastgir, DO (REGENXBIO) scAAV9.U7-ACCA – Kevin Flanigan, MD (Nationwide Children’s Hospital) SGT-001 – Carl Morris, PhD (Solid Biosciences) SRP-9001 – Teji Singh, MD (Sarepta Therapeutics) 3 years ago 2022 PPMD Annual Conference,Conferences & Meetings You may also like 56:09 Building Resilience: Overcoming Compassion Fatigue and Burnout 5 years ago 2020 PPMD Virtual Conference: Live Sessions,Conferences & Meetings 55:40 In the Pipeline: Restoring Dystrophin 5 years ago 2020 PPMD Virtual Conference: Live Sessions,Conferences & Meetings 42:58 In the Pipeline: Downstream Targets 5 years ago 2020 PPMD Virtual Conference: Live Sessions,Conferences & Meetings 1:03:52 Duchenne Care: Endocrinology in Duchenne 5 years ago 2020 PPMD Virtual Conference: Live Sessions,Conferences & Meetings 57:12 Duchenne Care: Acute Pulmonary Management 5 years ago 2020 PPMD Virtual Conference: Live Sessions,Conferences & Meetings 1:13:54 In the Pipeline: Gene Therapy 5 years ago 2020 PPMD Virtual Conference: Live Sessions,Conferences & Meetings gene therapy 1:32:13 Duchenne Care: Caring for Female Carriers of Duchenne 5 years ago 2020 PPMD Virtual Conference: Live Sessions,Conferences & Meetings 58:12 Keynote Address: Language Shapes our Landscape 5 years ago 2020 PPMD Virtual Conference: Live Sessions,Conferences & Meetings «1…1617181920…28»Page 18 of 28