August 30, 2018

Pfizer Terminates Domagrozumab (PF-06252616) Clinical Studies for the Treatment of Duchenne

We are deeply disappointed to learn that Pfizer is terminating two ongoing clinical studies evaluating domagrozumab (PF-06252616) for the treatment of Duchenne: a Phase 2 safety and efficacy study (B5161002) and an open-label extension study…

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August 29, 2018

One Month Till Game Day!

It’s the start of the football season and we want YOU to help your local team celebrate this year’s 11th Annual Coach To Cure MD! There’s still plenty of time for you to put together…

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August 23, 2018

Overview: Access to Unapproved Investigational Drugs in the U.S.

Overview: Access to Unapproved Investigational Drugs in the U.S.* Like you, PPMD has had many questions about the way we can access UNAPPROVED investigational therapies in Duchenne. Expanded access, compassionate use, Right to Try –…

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August 22, 2018

Go Casual for World Duchenne Awareness Day!

This year, celebrate World Duchenne Awareness Day on September 7 by hosting a Jeans Day at your school, group or office! Raise even more funds by getting your employer to match all donations that come in. You…

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August 22, 2018

ReveraGen Announces First Patient Enrollment in International Pivotal Trial of Vamorolone in Duchenne

  ReveraGen BioPharma announced the initiation and first patient enrollment in a double-blind, placebo- and prednisone-controlled clinical trial (VBP15-004) of vamorolone, a first-in-class dissociative steroidal anti-inflammatory, in Duchenne. This VISION-DMD study will enroll approximately 120…

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August 20, 2018

PPMD’s Certified Duchenne Care Center Program – August 2018 Bi-Annual Report

PPMD’s Certified Duchenne Care Center (CDCC) Program was developed to make comprehensive Duchenne care and services, provided in agreement with the CDC Care Considerations, available and accessible to as many families as possible, and to strengthen…

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August 16, 2018

Mitchell’s Run Thru Rockford Turns 20

For 20 years, residents of Rockford, Michigan have been supporting PPMD’s mission to end Duchenne by participating in Mitchell’s Run Thru Rockford. Created and organized by the Peterson family, in honor of their 22-year-old son Mitchell,…

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August 16, 2018

Join Our Team! Coach To Cure MD Returns 9/29/18

The 11th year of Coach To Cure MD returns September 29th and we need you and your family to join our team! Since we first huddled up 10 years ago, Coach To Cure MD has…

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August 16, 2018

Wave Life Sciences Receives US Orphan Drug and Rare Pediatric Disease Designations for WVE-210201

  Wave Life Sciences today announced that the FDA has granted both orphan drug designation and rare pediatric disease designation for WVE-210201 for the treatment of Duchenne. These designations represent the significant progress being made…

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August 8, 2018

Connect with other Duchenne Families in Your Area

Online interactions are great, but nothing can replace in-person connections with other families living with Duchenne. PPMD has local Connect groups all over the country for this very reason. Have you “connected” with your state’s PPMD Connect group…

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