Gene Therapy Approaches to Replace or Restore Dystrophin PF-06939926 – Kasia Lobello, MD (Pfizer, Inc.) RGX-202 – Jahannaz Dastgir, DO (REGENXBIO) scAAV9.U7-ACCA – Kevin Flanigan, MD (Nationwide Children’s Hospital) SGT-001 – Carl Morris, PhD (Solid Biosciences) SRP-9001 – Teji Singh, MD (Sarepta Therapeutics) 4 years ago 2022 PPMD Annual Conference,Conferences & Meetings You may also like 58:55 In the Pipeline: Gene Therapy 5 years ago 2021 PPMD Virtual Conference: Live Sessions,Conferences & Meetings 51:09 In the Pipeline: Reducing Inflammation 5 years ago 2021 PPMD Virtual Conference: Live Sessions,Conferences & Meetings 55:32 In the Pipeline: Improving the Heart and Mitochondria 5 years ago 2021 PPMD Virtual Conference: Live Sessions,Conferences & Meetings 1:10:27 In the Pipeline: Pre-Clinical Gene Therapy 5 years ago 2021 PPMD Virtual Conference: Live Sessions,Conferences & Meetings 47:59 In the Pipeline: Next-Gen Exon Skipping 5 years ago 2021 PPMD Virtual Conference: Live Sessions,Conferences & Meetings 15:59 Recently Reported Updates – NS Pharma 5 years ago 2021 PPMD Virtual Conference: Live Sessions,Conferences & Meetings 30:50 Recently Reported Updates – FibroGen 5 years ago 2021 PPMD Virtual Conference: Live Sessions,Conferences & Meetings 14:51 Recently Reported Updates – PTC Therapeutics 5 years ago 2021 PPMD Virtual Conference: Live Sessions,Conferences & Meetings «1…1415161718…28»Page 16 of 28