August 11, 2020

FibroGen Announces First Patient Enrolled in Pamrevlumab Phase 3 Clinical Trial

FibroGen, Inc. announced the initiation of LELANTOS, a Phase 3, randomized, double-blind, placebo-controlled trial of pamrevlumab or placebo in combination with systemic corticosteroids in patients with non-ambulatory Duchenne. PPMD is excited to see FibroGen’s continued…

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August 8, 2020

FDA Grants Accelerated Approval to Viltepso (viltolarsen)

PPMD is thrilled to learn that the FDA has granted accelerated approval to NS Pharma’s VILTEPSO™ (viltolarsen), a treatment of Duchenne in patients who have a confirmed mutation of the DMD gene that is amenable…

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August 7, 2020

WATCH: Family Friday – Do It Your Way & End Duchenne

Family Friday: Do It Your Way & End Duchenne Although COVID-19 has changed how we conduct events and socialize within our communities, it doesn’t change the fact that you can still support PPMD’s mission. Duchenne doesn’t…

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August 6, 2020

Have You Participated in a Clinical Trial That Was Terminated?

In an effort to learn more about the patient and family experience around clinical trials that have stopped or were terminated, PPMD and Duchenne UK have collaborated on a survey to learn more about your…

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August 6, 2020

NEW! Download PPMD’s Updated Education Matters Guides for Back-To-School

As the beginning of the school year quickly approaches, PPMD is working to support your family and help you plan for a successful classroom experience, whether it be in-person or virtual. We are thrilled to…

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August 6, 2020

PPMD Signs Onto Letter Urging Congress to Protect Immunocompromised Patients During the Pandemic

PPMD joined dozens of patient organizations in a letter to Congress urging them to protect immunocompromised patients during the pandemic. Americans living with compromised immune systems have routinely taken precautions in order to avoid becoming…

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August 4, 2020

ICYMI: Lunch & Learn Sessions

ICYMI: Lunch & Learn Sessions As part of this year’s Virtual Annual Conference, PPMD offered two Lunch & Learn Sessions where we were introduced to family assistance programs available to our community and we took…

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July 30, 2020

Did You Miss the PPMD Virtual Annual Conference?

Did You Miss the PPMD Virtual Annual Conference? PPMD’s first Virtual Annual Conference was incredible with nearly 2500 families, care providers, researchers, scientists, and industry partners joining us for four days of informative updates on…

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July 30, 2020

Join PPMD’s Back-To-School Webinar Series

Join PPMD’s Back-To-School Webinar Series Join us for PPMD’s back-to-school webinar series tackling questions and concerns the community has about both in-person and virtual learning environments. PPMD’s Care Team will be joined by leading experts…

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July 29, 2020

PPMD Announces Pediatric Certified Duchenne Care Center, Akron Children’s Hospital

Today Parent Project Muscular Dystrophy (PPMD) announced the expansion of our renowned Certified Duchenne Care Center Program (CDCCP) with the certification of the clinic at Akron Children’s Hospital (Akron Children’s) in Akron, Ohio. Rachel Schrader,…

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