June 14, 2018

A Game Night to End Duchenne

Game Night to End Duchenne in honor of Henry was a huge success last weekend! Raising close to $50,000 with no overhead costs, it was a night filled with close friends of the family and…

Learn More

June 13, 2018

End Duchenne Tour Recap: Birmingham, AL

PPMD was very happy to have the opportunity to meet the team from Children’s Hospital of Alabama and all of the families that came out to our End Duchenne Tour stop on June 6 in the…

Learn More

June 8, 2018

Sarepta Shares Quarterly Update, Including US Clinical Trial Updates

Sarepta has provided another quarterly update to the community, including information on their PPMO (Peptide Conjugated Phosphorodiamidate Morpholino Oligomer), an exon skipping technology designed to efficiently get inside cells, with the goal of producing more dystrophin in…

Learn More

June 6, 2018

Join the Race to End Duchenne

We are thrilled to announce the launch of the new name and look for our endurance program, Race to End Duchenne. This new name reflects the dynamic nature this program has taken on over the…

Learn More

June 5, 2018

Race Athlete Spotlight: Catie Sims

Catie Sims met Garrett Sapp and his family several years ago when she decided to turn her love of running into a way to help others. Since then she has become part of the Sapp…

Learn More

May 31, 2018

WATCH: Introducing PPMO – Webinar Recording with Sarepta Therapeutics

Sarepta Therapeutics, Inc. recently joined Parent Project Muscular Dystrophy (PPMD) for a community webinar update to discuss PPMO, Sarepta’s next generation precision RNA-targeting therapeutic platform for use in Duchenne muscular dystrophy. During the webinar, Sarepta…

Learn More

May 25, 2018

Race Recap: 2018 Walt Disney World Marathon Weekend

We’ve just returned from the Walt Disney World Marathon Weekend, which is where the Run For Our Sons program started, and wow what a weekend it was! From Sean Crosby’s inspirational talk at our Team…

Learn More

May 24, 2018

WATCH: Anti-Myostatin Adnectin RG6206 in Duchenne – Webinar Recording with Roche/Genentech

Roche/Genentech recently joined Parent Project Muscular Dystrophy for a webinar to provide an update on their Anti-Myostatin Adnectin (RG6206) development program. The team at Roche and its US affiliate, Genentech, and provided an overview of…

Learn More

May 18, 2018

Santhera Pharmaceuticals Launches Formal Expanded Access Program in the U.S.

PPMD is pleased to learn that Santhera Pharmaceuticals has launched a formal expanded access program in the U.S. for their investigational therapies, including idebenone. Learn more by visiting the Santhera website.

Learn More

May 14, 2018

The Duchenne Carrier Characterization Study at Nationwide Children’s Hospital

May is a month to celebrate mothers. PPMD’s dedication to mothers in our community is, in small part, reflected in our dedication to doing all we can to care for female carriers of Duchenne. The…

Learn More