Gene Therapy Approaches to Replace or Restore Dystrophin PF-06939926 – Kasia Lobello, MD (Pfizer, Inc.) RGX-202 – Jahannaz Dastgir, DO (REGENXBIO) scAAV9.U7-ACCA – Kevin Flanigan, MD (Nationwide Children’s Hospital) SGT-001 – Carl Morris, PhD (Solid Biosciences) SRP-9001 – Teji Singh, MD (Sarepta Therapeutics) 3 years ago 2022 PPMD Annual Conference,Conferences & Meetings You may also like 8:36 Here Is What I Hear — PPMD 2022 Annual Conference 3 years ago 2022 PPMD Annual Conference,Conferences & Meetings 39:20 The Future of Genetic Therapies — PPMD 2022 Annual Conference 3 years ago 2022 PPMD Annual Conference,Conferences & Meetings 25:56 Gene Therapy Era: What We Know — PPMD 2022 Annual Conference 3 years ago 2022 PPMD Annual Conference,Conferences & Meetings 32:14 Duchenne Siblings Panel: What We Want You To Know — PPMD 2022 Annual Meeting 3 years ago 2022 PPMD Annual Conference,Conferences & Meetings 34:37 Parent Panel: Things I’d Like My Doctor To Know — PPMD 2022 Annual Conference 3 years ago 2022 PPMD Annual Conference,Conferences & Meetings 1:10:31 Brain and Behavior — PPMD 2022 Annual Conference 3 years ago 2022 PPMD Annual Conference,Conferences & Meetings 32:27 New Learnings on Natural History — PPMD 2022 Annual Conference 3 years ago 2022 PPMD Annual Conference,Conferences & Meetings 47:30 Duchenne Landscape: Where We’ve Come From & How We’re Moving Forward — PPMD 2022 Annual Conference 3 years ago 2022 PPMD Annual Conference,Conferences & Meetings «1…1011121314…28»Page 12 of 28