Downstream (PPMD 2019 Conference) AGENDA 0:00 – Downstream Moderator: Lance Hester 1:25 – Roche/Genentech – Roxana Dreghici, MD 13:53 – Santhera – Kristina Nygren, MD 28:35 – FibroGen – Bassem Elmankabadi, MD 45:00 – Q&A 56:54 – POLLING QUESTIONS 7 years ago 2019 PPMD Annual Conference,Conferences & Meetings You may also like Exploring the Landscape of Gene Therapy – 2025 PPMD Annual Conference 1 year ago 2025 PPMD Annual Conference,Conferences & Meetings Trials & Treatments: Making Decisions that are Right for You – 2025 PPMD Annual Conference 1 year ago 2025 PPMD Annual Conference,Conferences & Meetings Building Friendships & Self Advocacy Skills – 2025 PPMD Annual Conference 1 year ago 2025 PPMD Annual Conference,Conferences & Meetings Keynote Address: Meeting the Challenge of Rare Disease – 2025 PPMD Annual Conference 1 year ago 2025 PPMD Annual Conference,Conferences & Meetings Approved Therapies & Sequential Therapy – PPMD 2025 Annual Conference 1 year ago 2025 PPMD Annual Conference,Conferences & Meetings How Do We Get to the Next Step in Research? The DCRN Explained – 2025 PPMD Annual Conference 1 year ago 2025 PPMD Annual Conference,Conferences & Meetings Dystrophin: The Missing Muscle Protein – 2025 PPMD Annual Conference 1 year ago 2025 PPMD Annual Conference,Conferences & Meetings Exercise: How Much is Too Much? – 2025 PPMD Annual Conference 1 year ago 2025 PPMD Annual Conference,Conferences & Meetings «12345…29»Page 3 of 29