July 8, 2025 /

Dystrophin: The Missing Muscle Protein – 2025 PPMD Annual Conference

Dystrophin: The Missing Muscle Protein

Moderator: Eric Camino, PhD

Understanding Dystrophin Expression Stan Nelson, MD

Dystrophin Restoration Pipeline Discussing Avidity Biosciences, Biomarin Pharmaceuticals, Dyne Therapeutics, Entrada Therapeutics, NS Pharma, Pepgen, WAVE Life Science – Kevin Flanigan, MD

From the Bench: Novel Approaches to Dystrophin Restoration – John Lueck, PhD


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