July 24, 2024 /

Current Approved Therapies Panel & Discussion (Pt. 2) – PPMD 2024 Annual Conference

Current Approved Therapies Panel Discussion Pt. 2: Broad Access to Gene Therapy

Rachel Schrader, MS, APRN, CPNP-PC, PPMD (Moderator)

Aravindhan Veerapandiayn, MD, Arkansas Children’s Hospital

Richard Shell, MD, Nationwide Children’s Hospital

Emma Ciafaloni, MD, University of Rochester

Kevin Flanigan, MD, Nationwide Children’s Hospital

Carol Wittlieb-Weber, MD, Children’s Hospital of Philadelphia

Larry Markham, MD, FAAP, FACC, Riley Children’s Hospital

Pat Furlong, Founding President & CEO, PPMD


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