Addressing the Complexities of Duchenne (PPMD 2019 Conference)

Addressing the Complexities of Duchenne – What You Should Know
Moderator: Anessa Fehsenfeld

• 0:10 – Attacking Duchenne from Every Angle – Anessa Fehsenfeld, PPMD Chairman
• 3:40 – Duchenne Research and Clinical Trials – Abby Bronson
  • Current therapeutic approaches and clinical trials
  • Strategies to accelerate the process
• 4:00 – Working to Facilitate a Favorable Access Environment – Annie Kennedy
  • Influencing policy and infrastructure that drives Duchenne research, treatments, and access
  • Producing evidence to reflect the Duchenne community’s experience to inform decision-making by all stakeholders within the access ecosystem
• 4:15 – Improvements in Care: Extending Quality of Life with a Focus on the Future – Kathi Kinnett
  • The Certified Duchenne Care Center network accomplishments
  • Integrating clinics, industry, and The Duchenne Registry to build a solid network
• 4:30 – The Patient Voice: Your Data Informing the Drug Development Ecosystem – Ryan Fischer
  • Your preferences and participation drives innovation and change
  • The Duchenne Registry and The Duchenne Outcomes Research Interchange
• 4:55p – POLLING QUESTIONS