December 21, 2023 / Advocacy,Clinical Trials,Research

PPMD & Community Partners Urge Timely, Transparent FDA Review of EMBARK Data

Today, PPMD joined the Best Day Ever Foundation, CureDuchenne, the Jett Foundation, the Little Hercules Foundation, The Muscular Dystrophy Family Foundation, and Team Joseph in sending a letter to the Federal Drug Administration (FDA) regarding the ongoing review of EMBARK trial data for ELEVIDYS. The letter acknowledged the difficulty in measuring and evaluating Duchenne disease progression in a relatively short study period, but also urged a timely and transparent review of the data.

We recognize and value how the FDA has incorporated the patient perspectives throughout this decision-making process and encourage continued engagement as the review moves forward in an expedited and inclusive manner.

You can read the full text of the letter here.

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