May 7, 2020

Solid Biosciences Shares Update on SGT-001 Phase I/II Clinical Hold for IGNITE DMD Program

Solid Biosciences shared today that their IGNITE DMD Phase I/II clinical trial will remain on clinical hold. Solid will continue to work with the FDA to provide further data and analyses relating to their manufacturing…

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May 1, 2020

PPMD’s Annual Conference to Go Virtual this July

PPMD’s Annual Conference to Go Virtual this July PPMD has made the difficult decision to change the format of our Annual Conference this summer, previously set to be an in-person meeting in July in Arizona….

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May 1, 2020

WATCH: Family Friday – Managing Learning Challenges at Home

Family Friday: Managing Learning Challenges at Home For many of us, self-quarantine is in full swing, and adjusting to a different family structure may be overwhelming. So your PPMD family is launching Family Fridays to…

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May 1, 2020

NEW REPORT: COVID-19 & Duchenne/Becker Muscular Dystrophy

NEW REPORT: COVID-19 & Duchenne/Becker Muscular Dystrophy Since 2014, PPMD has been growing its network of Certified Duchenne Care Centers (CDCCs) with the goal of standardizing and optimizing patient care throughout the US and making…

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May 1, 2020

New Video: Meet The Duchenne Registry App!

New Video: Meet The Duchenne Registry App! Have you downloaded The Duchenne Registry app? Is your account updated? Now’s the time to join the world’s largest Duchenne-specific registry and be the first to learn about…

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April 30, 2020

WATCH: Access to Approved Therapies and Home Care

Webinar Recording: Access to Approved Therapies and Home Care During our interactive webinar on April 29, 2020, we discussed access to approved therapies and home health considerations in the midst of a pandemic. Speakers from…

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April 27, 2020

Italfarmaco Provides Update on Advanced-Stage Clinical Development Program with Givinostat in Duchenne

Good news from Italfarmaco! As discussed on our webinar last week, an Independent Data Monitoring Committee (IDMC) has recommended the continuation of their Phase 3 Givinostat trial, determining that the trial is not futile. They…

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April 27, 2020

WATCH: Italfarmaco Provides Givinostat Update

Webinar Recording: Italfarmaco Provides Givinostat Update On April 22, 2020, Italfarmaco joined PPMD for a webinar to update the community about Italfarmaco’s development of Givinostat and the recent results of the futility analysis of the…

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April 24, 2020

WATCH: Family Friday – Healthy & Fun Cooking at Home

Family Friday: Healthy & Fun Cooking at Home For many of us, self-quarantine is in full swing, and adjusting to a different family structure may be overwhelming. So your PPMD family is launching Family Fridays…

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April 21, 2020

New Charitable Income Tax Deduction Further Incentivizes Your Gift to PPMD

COVID-19 may have altered our lives, but not our priorities. PPMD needs your help now to continue to fund the fight to end Duchenne. And thanks to the recently enacted stimulus bill, known as the…

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