July 6, 2021

Recently Reported Updates from PPMD’s 2021 Virtual Annual Conference

PPMD’s 2021 Virtual Annual Conference: Recently Reported Updates As a new addition to PPMD’s 2021 Virtual Conference, PPMD invited industry partners to share new data with the community live during the Conference in a series…

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July 1, 2021

PPMD Is Moving to Washington, DC!

PPMD’s Main Office is Moving to Washington, DC! When Parent Project Muscular Dystrophy started in 1994, formed by a small group of parents and grandparents out of Ohio, we knew that one of our first…

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June 30, 2021

Rewatch PPMD’s 2021 Virtual Annual Conference

Did You Miss PPMD’s 2021 Virtual Annual Conference? PPMD’s 2021 Virtual Annual Conference was incredible with close to 2,000 families, care providers, researchers, scientists, and industry partners joining us for four days of informative updates…

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June 26, 2021

Italfarmaco Announces Topline Data from Phase 2 Trial with Givinostat in Patients with Becker

This afternoon at PPMD’s Virtual Annual Conference, Italfarmaco shared Phase II Study results from the Givinostat trial in patients with Becker. They also issued a press release below. Although they did not meet the primary…

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June 17, 2021

PPMD Virtual Conference to Feature 5 Late-Breaking News Sessions

PPMD’s 2021 Virtual Annual Conference to Feature Five Late-Breaking News Sessions We are excited to share that five Industry Partners will be announcing newly released data to the Duchenne community for the first time during…

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June 16, 2021

PPMD & Jesse’s Journey Award $172,000 (CAD) Clinical Fellowship in Duchenne Endocrinology & Bone Fragility

Parent Project Muscular Dystrophy (PPMD) and Jesse’s Journey today announced a collaborative research award of $172,000 (CAD) in support of a two-year Clinical Fellowship in Duchenne Endocrinology and Bone Fragility. The award will sponsor the fellowship of…

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June 14, 2021

PPMD’s Virtual Conference Hub is Live!

PPMD’s 2021 Virtual Annual Conference – Our Hub is Live! If you haven’t registered for PPMD’s 2021 Virtual Annual Conference — now’s the time to do so! Our Conference Hub is now open! This is your opportunity…

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June 11, 2021

WATCH: SRP-9001 Micro-Dystrophin Gene Therapy Clinical Update (Webinar Recording)

WATCH: SRP-9001 Micro-Dystrophin Gene Therapy Clinical Update Parent Project Muscular Dystrophy was joined by Sarepta Therapeutics for a webinar update on June 2, 2021. Sarepta was invited to present recent updates from their ongoing clinical…

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June 8, 2021

WATCH: Connect with the Experts – Navigating the College Campus with Duchenne

PPMD’s Rachel Schrader and Mena Scavina recently moderated a fantastic Connect with the Experts: Navigating the College Campus with Duchenne webinar. They led a dynamic conversation around what the college experience may look like for…

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June 1, 2021

Santhera & ReveraGen Announce Positive & Statistically Significant Topline Results in VISION-DMD Study

Santhera and ReveraGen today announced positive and statistically significant results from the 24-week readout of the VISION-DMD study of vamorolone in Duchenne. The companies report that study demonstrated strong efficacy across primary and secondary endpoints…

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