The Complexities of Duchenne (PPMD 2019 Conference) AGENDA 1:40-3:15p – The Complexities of Duchenne Moderator: Pat Furlong 1:40 – Duchenne: A Multisystem Disease – Stan Nelson, MD, PhD 2:00 – Variability: Modifiers to the Gene – Kevin Flanigan, MD 2:20 – Measuring Outcomes in the Face of Variability – Cliff Bechtold 2:40 – Challenges in Designing Trials – Craig McDonald, MD 3:00 – Q&A 7 years ago 2019 PPMD Annual Conference,Conferences & Meetings You may also like 1:30:45 Panel Discussion: Looking Ahead to Combination Therapies — PPMD 2022 Annual Conference 4 years ago 2022 PPMD Annual Conference,Conferences & Meetings 1:22:12 Caring for the Caregiver of Teens & Adults Living with Duchenne — PPMD 2022 Annual Conference 4 years ago 2022 PPMD Annual Conference,Conferences & Meetings 28:44 Strategies for Mitigating Inflammation and Fibrosis — PPMD 2022 Annual Conference 4 years ago 2022 PPMD Annual Conference,Conferences & Meetings 17:46 Late Breaking News: Capricor / Cap-1002 — PPMD 2022 Annual Conference 4 years ago 2022 PPMD Annual Conference,Conferences & Meetings 20:30 Late-Breaking News: Italfarmaco / Givionstat — PPMD 2022 Annual Conference 4 years ago 2022 PPMD Annual Conference,Conferences & Meetings 25:46 Late Breaking News: Ataluren / Translarna — PPMD 2022 Annual Conference 4 years ago 2022 PPMD Annual Conference,Conferences & Meetings 1:40:53 Restoring Dystrophin via Exon Skipping Strategies — PPMD 2022 Annual Conference 4 years ago 2022 PPMD Annual Conference,Conferences & Meetings 57:08 Novel Approaches for Combatting Duchenne — PPMD 2022 Annual Conference 4 years ago 2022 PPMD Annual Conference,Conferences & Meetings «1…1011121314…29»Page 12 of 29