Restoring Dystrophin via Exon Skipping Strategies AOC 1044 – Mark Stahl, MD (Avidity Biosciences) BMN 351 – Dave Jacoby MD, PhD (BioMarin Pharmaceutical Inc.) DYNE-251 – Ash Dugar, PhD, MBA (Dyne Therapeutics) ED051 – Michelle Mellion, MD (PepGen, Inc.) ENTR-601-44 – Nerissa Kreher, MD, MBA (Entrada Therapeutics) SRP-5051 – Teji Singh, MD (Sarepta Therapeutics) WVE-N531 – Mike Panzara, MD, MPH (Wave Life Sciences) 3 years ago 2022 PPMD Annual Conference,Conferences & Meetings You may also like 59:20 CRISPR: Future Strategies in Gene Therapy (PPMD 2019 Conference) 7 years ago 2019 PPMD Annual Conference,Conferences & Meetings gene therapy 33:56 Understanding Immunity (PPMD 2019 Conference) 7 years ago 2019 PPMD Annual Conference,Conferences & Meetings 1:28:49 Gene Correction (PPMD 2019 Conference) 7 years ago 2019 PPMD Annual Conference,Conferences & Meetings 1:40:24 Our Voice Matters: Duchenne Town Hall Forum (PPMD 2019 Conference) 7 years ago 2019 PPMD Annual Conference,Conferences & Meetings «1…262728Page 28 of 28