Research Row: Approved or on the Horizon Join us as we discuss Approved Therapies and those on the Horizon of approval. Santhera Pharmaceuticals (Vamorolone) Italfarmaco ( Givinostat) PTC Pharmaceuticals (Ataluren, Emflaza) Sarepta Therapeutics (Amondys45, Exondys 51, Vyondys53) NS Pharma (Viltepso) 3 years ago 2023 PPMD Annual Conference,Conferences & Meetings You may also like 8:36 Here Is What I Hear — PPMD 2022 Annual Conference 3 years ago 2022 PPMD Annual Conference,Conferences & Meetings 39:20 The Future of Genetic Therapies — PPMD 2022 Annual Conference 3 years ago 2022 PPMD Annual Conference,Conferences & Meetings 1:30:40 Gene Therapy Approaches to Replace or Restore Dystrophin — PPMD 2022 Annual Conference 3 years ago 2022 PPMD Annual Conference,Conferences & Meetings 25:56 Gene Therapy Era: What We Know — PPMD 2022 Annual Conference 3 years ago 2022 PPMD Annual Conference,Conferences & Meetings 32:14 Duchenne Siblings Panel: What We Want You To Know — PPMD 2022 Annual Meeting 3 years ago 2022 PPMD Annual Conference,Conferences & Meetings 34:37 Parent Panel: Things I’d Like My Doctor To Know — PPMD 2022 Annual Conference 3 years ago 2022 PPMD Annual Conference,Conferences & Meetings 1:10:31 Brain and Behavior — PPMD 2022 Annual Conference 3 years ago 2022 PPMD Annual Conference,Conferences & Meetings 32:27 New Learnings on Natural History — PPMD 2022 Annual Conference 3 years ago 2022 PPMD Annual Conference,Conferences & Meetings «1…1011121314…28»Page 12 of 28