Research Row: Approved or on the Horizon Join us as we discuss Approved Therapies and those on the Horizon of approval. Santhera Pharmaceuticals (Vamorolone) Italfarmaco ( Givinostat) PTC Pharmaceuticals (Ataluren, Emflaza) Sarepta Therapeutics (Amondys45, Exondys 51, Vyondys53) NS Pharma (Viltepso) 3 years ago 2023 PPMD Annual Conference,Conferences & Meetings You may also like 1:36:49 Duchenne Cardiac Care: PPMD Cardiac Care Meeting Learnings — PPMD 2022 Annual Conference 4 years ago 2022 PPMD Annual Conference,Conferences & Meetings 1:18:24 Panel Discussion: Facilitating Independence — PPMD 2022 Annual Conference 4 years ago 2022 PPMD Annual Conference,Conferences & Meetings 31:10 The Landscape of Cardiac Care: Emerging Therapies on the Horizon — PPMD 2022 Annual Conference 4 years ago 2022 PPMD Annual Conference,Conferences & Meetings 54:15 Emergency Care in Duchenne — PPMD 2022 Annual Conference 4 years ago 2022 PPMD Annual Conference,Conferences & Meetings 8:36 Here Is What I Hear — PPMD 2022 Annual Conference 4 years ago 2022 PPMD Annual Conference,Conferences & Meetings 39:20 The Future of Genetic Therapies — PPMD 2022 Annual Conference 4 years ago 2022 PPMD Annual Conference,Conferences & Meetings 1:30:40 Gene Therapy Approaches to Replace or Restore Dystrophin — PPMD 2022 Annual Conference 4 years ago 2022 PPMD Annual Conference,Conferences & Meetings 25:56 Gene Therapy Era: What We Know — PPMD 2022 Annual Conference 4 years ago 2022 PPMD Annual Conference,Conferences & Meetings «1…1112131415…30»Page 13 of 30