Italfarmaco Provides Givinostat Update (March 2019) Italfarmaco joined PPMD for a webinar on March 27, 2019 to update the community about Italfarmaco’s development of Givinostat and currently enrolling Phase 3 confirmatory study in Duchenne muscular dystrophy. 7 years ago Research & Clinical Trial Webinars,Webinars You may also like 29:52 Webinar: Duchenne Newborn Screening – Next Steps Following ACHDNC Dissolution 11 months ago Webinars newborn screening 59:32 Webinar: Wave Life Sciences – Update on FORWARD-53 Study of WVE-N531 11 months ago Research & Clinical Trial Webinars,Webinars wave life sciences,WVE-N531 1:00:09 Webinar: Avidity Biosciences – Topline Data from EXPLORE44® Clinical Trial 12 months ago Research & Clinical Trial Webinars,Webinars AOC 1044,avidity biosciences,del-zota 47:43 Webinar: Capricor Therapeutics – Update on Deramiocel for Cardiomyopathy in Patients with Duchenne 1 year ago Research & Clinical Trial Webinars,Webinars cap-1002,capricor,cardiac,deramiocel 02:15:11 PPMD’s Duchenne Early Intervention Symposium 1 year ago Webinars newborn screening 01:08:05 Webinar: Solid Biosciences – Update on Gene Therapy Candidate SGT-003 1 year ago Research & Clinical Trial Webinars,Webinars gene therapy,sgt-003,solid biosciences 58:14 Webinar: Sevasemten – CANYON Trial Topline Results 1 year ago Research & Clinical Trial Webinars,Webinars edg-5506,edgewise 1:01:40 Webinar: RGX-202 – AFFINITY DUCHENNE Pivotal Program and Functional Data 1 year ago Research & Clinical Trial Webinars,Webinars gene therapy,RGX-202 «12345…28»Page 3 of 28