Gene Therapy: What We Know Today & Will Need to Know Tomorrow (PPMD 2019 Conference) 8:10a – POLLING QUESTIONS 8:15-9:30a – Gene Therapy: What We Know Today & What We Will Need to Know Tomorrow Moderator: Tim Cripe – 8:15 – Understanding Gene Therapy – What We Know Today – Barry Byrne MD, PhD – 8:35 – Panel Discussion: Current Hurdles in Gene Therapy Moderator: Tim Cripe, MD Panel: Lee Sweeney, Kevin Flanigan, Kathryn Wagner, Barry Byrne – 9:10 – Q&A 7 years ago 2019 PPMD Annual Conference,Conferences & Meetings You may also like Finding Light in the Journey: Fostering Resilience, Gratitude & Hope – 2025 PPMD Annual Conference 1 year ago 2025 PPMD Annual Conference,Conferences & Meetings Cardiac Management Throughout the Lifespan – 2025 PPMD Annual Conference 1 year ago 2025 PPMD Annual Conference,Conferences & Meetings Taking Charge of Your Future: A PAAC Presentation – 2025 PPMD Annual Conference 1 year ago 2025 PPMD Annual Conference,Conferences & Meetings Webinar: Sarepta Therapeutics – Safety Update on ELEVIDYS in Non-Ambulatory Individuals Living with Duchenne 1 year ago Research & Clinical Trial Webinars,Webinars elevidys,gene therapy,sarepta 1:20:43 Webinar: Sarepta Therapeutics – Duchenne Gene Therapy Update 1 year ago Research & Clinical Trial Webinars,Webinars elevidys,gene therapy,sarepta 01:08:05 Webinar: Solid Biosciences – Update on Gene Therapy Candidate SGT-003 1 year ago Research & Clinical Trial Webinars,Webinars gene therapy,sgt-003,solid biosciences 1:01:40 Webinar: RGX-202 – AFFINITY DUCHENNE Pivotal Program and Functional Data 2 years ago Research & Clinical Trial Webinars,Webinars gene therapy,RGX-202 39:21 30 Years Fighting for Every Future: Opening Remarks from Pat Furlong – PPMD 2024 Annual Conference 2 years ago 2024 PPMD Annual Conference,Conferences & Meetings «1…34567…31»Page 5 of 31