Gene Therapy Trials (PPMD 2019 Conference) AGENDA 0:00 – Gene Therapy Trials Moderator: Richard Klein 2:08 – Solid – Genevieve A. Laforet, MD, PhD 24:02 – Pfizer – Michael Binks, MD 46:42 – Sarepta – Doug Ingram 1:11:24 – Q&A 1:42:25 – POLLING QUESTIONS 7 years ago 2019 PPMD Annual Conference,Conferences & Meetings You may also like Therapies That Slow Progression – 2025 PPMD Annual Conference 6 months ago 2025 PPMD Annual Conference,Conferences & Meetings A New Take on the Ins and Outs – 2025 PPMD Annual Conference 6 months ago 2025 PPMD Annual Conference,Conferences & Meetings How MRI is Advancing Drug Development for Duchenne – 2025 PPMD Annual Conference 6 months ago 2025 PPMD Annual Conference,Conferences & Meetings Finding Light in the Journey: Fostering Resilience, Gratitude & Hope – 2025 PPMD Annual Conference 6 months ago 2025 PPMD Annual Conference,Conferences & Meetings Cardiac Management Throughout the Lifespan – 2025 PPMD Annual Conference 6 months ago 2025 PPMD Annual Conference,Conferences & Meetings Taking Charge of Your Future: A PAAC Presentation – 2025 PPMD Annual Conference 6 months ago 2025 PPMD Annual Conference,Conferences & Meetings Webinar: Sarepta Therapeutics – Safety Update on ELEVIDYS in Non-Ambulatory Individuals Living with Duchenne 7 months ago Research & Clinical Trial Webinars,Webinars elevidys,gene therapy,sarepta 1:20:43 Webinar: Sarepta Therapeutics – Duchenne Gene Therapy Update 8 months ago Research & Clinical Trial Webinars,Webinars elevidys,gene therapy,sarepta «12345…30»Page 3 of 30