Gene Therapy Trials (PPMD 2019 Conference) AGENDA 0:00 – Gene Therapy Trials Moderator: Richard Klein 2:08 – Solid – Genevieve A. Laforet, MD, PhD 24:02 – Pfizer – Michael Binks, MD 46:42 – Sarepta – Doug Ingram 1:11:24 – Q&A 1:42:25 – POLLING QUESTIONS 2019 PPMD Annual Conference,Conferences & Meetings 6 years ago You may also like Approved Therapies & Sequential Therapy – PPMD 2025 Annual Conference 2 days ago 2025 PPMD Annual Conference,Conferences & Meetings How Do We Get to the Next Step in Research? The DCRN Explained – 2025 PPMD Annual Conference 2 days ago 2025 PPMD Annual Conference,Conferences & Meetings Dystrophin: The Missing Muscle Protein – 2025 PPMD Annual Conference 2 days ago 2025 PPMD Annual Conference,Conferences & Meetings Exercise: How Much is Too Much? – 2025 PPMD Annual Conference 2 days ago 2025 PPMD Annual Conference,Conferences & Meetings Navigating Behaviors: Strategies for Support & Success – 2025 PPMD Annual Conference 2 days ago 2025 PPMD Annual Conference,Conferences & Meetings Nurturing Mental Wellness in Everyday Life – 2025 PPMD Annual Conference 2 days ago 2025 PPMD Annual Conference,Conferences & Meetings Updates in Research & Care for Carriers – 2025 PPMD Annual Conference 2 days ago 2025 PPMD Annual Conference,Conferences & Meetings Therapies That Slow Progression – 2025 PPMD Annual Conference 2 days ago 2025 PPMD Annual Conference,Conferences & Meetings «1234…30»Page 2 of 30