Restoring Dystrophin via Exon Skipping Strategies AOC 1044 – Mark Stahl, MD (Avidity Biosciences) BMN 351 – Dave Jacoby MD, PhD (BioMarin Pharmaceutical Inc.) DYNE-251 – Ash Dugar, PhD, MBA (Dyne Therapeutics) ED051 – Michelle Mellion, MD (PepGen, Inc.) ENTR-601-44 – Nerissa Kreher, MD, MBA (Entrada Therapeutics) SRP-5051 – Teji Singh, MD (Sarepta Therapeutics) WVE-N531 – Mike Panzara, MD, MPH (Wave Life Sciences) 4 years ago 2022 PPMD Annual Conference,Conferences & Meetings You may also like 47:59 In the Pipeline: Next-Gen Exon Skipping 5 years ago 2021 PPMD Virtual Conference: Live Sessions,Conferences & Meetings 15:59 Recently Reported Updates – NS Pharma 5 years ago 2021 PPMD Virtual Conference: Live Sessions,Conferences & Meetings 30:50 Recently Reported Updates – FibroGen 5 years ago 2021 PPMD Virtual Conference: Live Sessions,Conferences & Meetings 14:51 Recently Reported Updates – PTC Therapeutics 5 years ago 2021 PPMD Virtual Conference: Live Sessions,Conferences & Meetings 22:48 Recently Reported Updates – Italfarmaco 5 years ago 2021 PPMD Virtual Conference: Live Sessions,Conferences & Meetings 24:20 Recently Reported Updates – ReveraGen 5 years ago 2021 PPMD Virtual Conference: Live Sessions,Conferences & Meetings 3:09:41 2021 Advocacy in Action: Virtual Town Hall 5 years ago Conferences & Meetings 15:06 Welcome Address: Duchenne Today 6 years ago 2020 PPMD Virtual Conference: Live Sessions,Conferences & Meetings «1…1617181920…29»Page 18 of 29