Research Row: Approved or on the Horizon Join us as we discuss Approved Therapies and those on the Horizon of approval. Santhera Pharmaceuticals (Vamorolone) Italfarmaco ( Givinostat) PTC Pharmaceuticals (Ataluren, Emflaza) Sarepta Therapeutics (Amondys45, Exondys 51, Vyondys53) NS Pharma (Viltepso) 2023 PPMD Annual Conference,Conferences & Meetings 2 years ago You may also like Approved Therapies & Sequential Therapy – PPMD 2025 Annual Conference 2 days ago 2025 PPMD Annual Conference,Conferences & Meetings How Do We Get to the Next Step in Research? The DCRN Explained – 2025 PPMD Annual Conference 2 days ago 2025 PPMD Annual Conference,Conferences & Meetings Dystrophin: The Missing Muscle Protein – 2025 PPMD Annual Conference 2 days ago 2025 PPMD Annual Conference,Conferences & Meetings Exercise: How Much is Too Much? – 2025 PPMD Annual Conference 2 days ago 2025 PPMD Annual Conference,Conferences & Meetings Navigating Behaviors: Strategies for Support & Success – 2025 PPMD Annual Conference 2 days ago 2025 PPMD Annual Conference,Conferences & Meetings Nurturing Mental Wellness in Everyday Life – 2025 PPMD Annual Conference 2 days ago 2025 PPMD Annual Conference,Conferences & Meetings Updates in Research & Care for Carriers – 2025 PPMD Annual Conference 2 days ago 2025 PPMD Annual Conference,Conferences & Meetings Therapies That Slow Progression – 2025 PPMD Annual Conference 2 days ago 2025 PPMD Annual Conference,Conferences & Meetings «1234…28»Page 2 of 28