Gene Therapy Trials (PPMD 2019 Conference) AGENDA 0:00 – Gene Therapy Trials Moderator: Richard Klein 2:08 – Solid – Genevieve A. Laforet, MD, PhD 24:02 – Pfizer – Michael Binks, MD 46:42 – Sarepta – Doug Ingram 1:11:24 – Q&A 1:42:25 – POLLING QUESTIONS 2019 PPMD Annual Conference,Conferences & Meetings 6 years ago You may also like 38:43 DPT Meeting: FDA Opening Remarks 6 years ago 2019 Duchenne Platform Trial Stakeholder Meeting,Conferences & Meetings 23:02 DPT Meeting: DPT Protocol in Practice 6 years ago 2019 Duchenne Platform Trial Stakeholder Meeting,Conferences & Meetings 43:44 DPT Meeting: Overview of DPT Proposed Protocol 6 years ago 2019 Duchenne Platform Trial Stakeholder Meeting,Conferences & Meetings 49:36 DPT Meeting: Panel 1 – Protocol Objectives & Eligibility 6 years ago 2019 Duchenne Platform Trial Stakeholder Meeting,Conferences & Meetings 1:07:15 DPT Meeting: Panel 2 – Endpoints & Schedule of Events 6 years ago 2019 Duchenne Platform Trial Stakeholder Meeting,Conferences & Meetings 44:50 DPT Meeting: Panel 3 – Operations & Governance 6 years ago 2019 Duchenne Platform Trial Stakeholder Meeting,Conferences & Meetings 1:02:36 DPT Meeting: Parent Commentary & Advocacy Perspective 6 years ago 2019 Duchenne Platform Trial Stakeholder Meeting,Conferences & Meetings 18:59 DPT Meeting: Key Takeaways & Next Steps 6 years ago 2019 Duchenne Platform Trial Stakeholder Meeting,Conferences & Meetings «1…2425262728…30»Page 26 of 30