Gene Therapy Trials (PPMD 2019 Conference) AGENDA 0:00 – Gene Therapy Trials Moderator: Richard Klein 2:08 – Solid – Genevieve A. Laforet, MD, PhD 24:02 – Pfizer – Michael Binks, MD 46:42 – Sarepta – Doug Ingram 1:11:24 – Q&A 1:42:25 – POLLING QUESTIONS 7 years ago 2019 PPMD Annual Conference,Conferences & Meetings You may also like 1:22:12 Caring for the Caregiver of Teens & Adults Living with Duchenne — PPMD 2022 Annual Conference 4 years ago 2022 PPMD Annual Conference,Conferences & Meetings 28:44 Strategies for Mitigating Inflammation and Fibrosis — PPMD 2022 Annual Conference 4 years ago 2022 PPMD Annual Conference,Conferences & Meetings 17:46 Late Breaking News: Capricor / Cap-1002 — PPMD 2022 Annual Conference 4 years ago 2022 PPMD Annual Conference,Conferences & Meetings 20:30 Late-Breaking News: Italfarmaco / Givionstat — PPMD 2022 Annual Conference 4 years ago 2022 PPMD Annual Conference,Conferences & Meetings 25:46 Late Breaking News: Ataluren / Translarna — PPMD 2022 Annual Conference 4 years ago 2022 PPMD Annual Conference,Conferences & Meetings 1:40:53 Restoring Dystrophin via Exon Skipping Strategies — PPMD 2022 Annual Conference 4 years ago 2022 PPMD Annual Conference,Conferences & Meetings 57:08 Novel Approaches for Combatting Duchenne — PPMD 2022 Annual Conference 4 years ago 2022 PPMD Annual Conference,Conferences & Meetings 1:36:49 Duchenne Cardiac Care: PPMD Cardiac Care Meeting Learnings — PPMD 2022 Annual Conference 4 years ago 2022 PPMD Annual Conference,Conferences & Meetings «1…1112131415…31»Page 13 of 31