Gene Therapy Trials (PPMD 2019 Conference) AGENDA 0:00 – Gene Therapy Trials Moderator: Richard Klein 2:08 – Solid – Genevieve A. Laforet, MD, PhD 24:02 – Pfizer – Michael Binks, MD 46:42 – Sarepta – Doug Ingram 1:11:24 – Q&A 1:42:25 – POLLING QUESTIONS 2019 PPMD Annual Conference,Conferences & Meetings 6 years ago You may also like Stronger Together: Empowering Families Through Community, Care, and Research – 2025 PPMD Annual Conference 2 weeks ago 2025 PPMD Annual Conference,Conferences & Meetings A New Era of Steroids, Endocrinology & Emergency Care – 2025 PPMD Annual Conference 2 weeks ago 2025 PPMD Annual Conference,Conferences & Meetings Opening Session: A New Era in Duchenne & Becker Muscular Dystrophy – 2025 PPMD Annual Conference 2 weeks ago 2025 PPMD Annual Conference,Conferences & Meetings The Impact of Diagnosis: Managing Family Dynamics – 2025 PPMD Annual Conference 2 weeks ago 2025 PPMD Annual Conference,Conferences & Meetings Exploring the Landscape of Gene Therapy – 2025 PPMD Annual Conference 2 weeks ago 2025 PPMD Annual Conference,Conferences & Meetings Trials & Treatments: Making Decisions that are Right for You – 2025 PPMD Annual Conference 2 weeks ago 2025 PPMD Annual Conference,Conferences & Meetings Building Friendships & Self Advocacy Skills – 2025 PPMD Annual Conference 2 weeks ago 2025 PPMD Annual Conference,Conferences & Meetings Keynote Address: Meeting the Challenge of Rare Disease – 2025 PPMD Annual Conference 2 weeks ago 2025 PPMD Annual Conference,Conferences & Meetings 123…30»Page 1 of 30