The Power of Advocacy and Real World Evidence to inform an FDA Advisory Committee on Gene Therapy for DMD Craig McDonald, MD 3 years ago 2023 PPMD Annual Conference,Conferences & Meetings You may also like 1:40:24 Our Voice Matters: Duchenne Town Hall Forum (PPMD 2019 Conference) 7 years ago 2019 PPMD Annual Conference,Conferences & Meetings «1…282930Page 30 of 30