Gene Correction (PPMD 2019 Conference) 0:00 – Gene Correction Moderator: Richard Klein 1:16 – PTC – Richard Able Jr., PhD 20:30 – Sarepta – Gilmore O’Neill, M.B., M.M.SC. 38:57 – Wave – Michael Panzara, MD, MPH 59:13 – NS Pharma – Leslie Magnus, MD 1:10:36 – Q&A 1:23:36 – POLLING QUESTIONS 7 years ago 2019 PPMD Annual Conference,Conferences & Meetings You may also like Exploring the Landscape of Gene Therapy – 2025 PPMD Annual Conference 1 year ago 2025 PPMD Annual Conference,Conferences & Meetings Trials & Treatments: Making Decisions that are Right for You – 2025 PPMD Annual Conference 1 year ago 2025 PPMD Annual Conference,Conferences & Meetings Building Friendships & Self Advocacy Skills – 2025 PPMD Annual Conference 1 year ago 2025 PPMD Annual Conference,Conferences & Meetings Keynote Address: Meeting the Challenge of Rare Disease – 2025 PPMD Annual Conference 1 year ago 2025 PPMD Annual Conference,Conferences & Meetings Approved Therapies & Sequential Therapy – PPMD 2025 Annual Conference 1 year ago 2025 PPMD Annual Conference,Conferences & Meetings How Do We Get to the Next Step in Research? The DCRN Explained – 2025 PPMD Annual Conference 1 year ago 2025 PPMD Annual Conference,Conferences & Meetings Dystrophin: The Missing Muscle Protein – 2025 PPMD Annual Conference 1 year ago 2025 PPMD Annual Conference,Conferences & Meetings Exercise: How Much is Too Much? – 2025 PPMD Annual Conference 1 year ago 2025 PPMD Annual Conference,Conferences & Meetings «12345…29»Page 3 of 29