Gene Correction (PPMD 2019 Conference) 0:00 – Gene Correction Moderator: Richard Klein 1:16 – PTC – Richard Able Jr., PhD 20:30 – Sarepta – Gilmore O’Neill, M.B., M.M.SC. 38:57 – Wave – Michael Panzara, MD, MPH 59:13 – NS Pharma – Leslie Magnus, MD 1:10:36 – Q&A 1:23:36 – POLLING QUESTIONS 2019 PPMD Annual Conference,Conferences & Meetings 6 years ago You may also like Stronger Together: Empowering Families Through Community, Care, and Research – 2025 PPMD Annual Conference 1 week ago 2025 PPMD Annual Conference,Conferences & Meetings A New Era of Steroids, Endocrinology & Emergency Care – 2025 PPMD Annual Conference 1 week ago 2025 PPMD Annual Conference,Conferences & Meetings Opening Session: A New Era in Duchenne & Becker Muscular Dystrophy – 2025 PPMD Annual Conference 1 week ago 2025 PPMD Annual Conference,Conferences & Meetings The Impact of Diagnosis: Managing Family Dynamics – 2025 PPMD Annual Conference 1 week ago 2025 PPMD Annual Conference,Conferences & Meetings Exploring the Landscape of Gene Therapy – 2025 PPMD Annual Conference 1 week ago 2025 PPMD Annual Conference,Conferences & Meetings Trials & Treatments: Making Decisions that are Right for You – 2025 PPMD Annual Conference 1 week ago 2025 PPMD Annual Conference,Conferences & Meetings Building Friendships & Self Advocacy Skills – 2025 PPMD Annual Conference 1 week ago 2025 PPMD Annual Conference,Conferences & Meetings Keynote Address: Meeting the Challenge of Rare Disease – 2025 PPMD Annual Conference 1 week ago 2025 PPMD Annual Conference,Conferences & Meetings 123…28»Page 1 of 28