Gene Correction (PPMD 2019 Conference) 0:00 – Gene Correction Moderator: Richard Klein 1:16 – PTC – Richard Able Jr., PhD 20:30 – Sarepta – Gilmore O’Neill, M.B., M.M.SC. 38:57 – Wave – Michael Panzara, MD, MPH 59:13 – NS Pharma – Leslie Magnus, MD 1:10:36 – Q&A 1:23:36 – POLLING QUESTIONS 6 years ago 2019 PPMD Annual Conference,Conferences & Meetings You may also like 27:24 Our Stories Matter – Buddy Cassidy (PPMD 2019 Conference) 6 years ago 2019 PPMD Annual Conference,Conferences & Meetings 59:20 CRISPR: Future Strategies in Gene Therapy (PPMD 2019 Conference) 6 years ago 2019 PPMD Annual Conference,Conferences & Meetings gene therapy 33:56 Understanding Immunity (PPMD 2019 Conference) 6 years ago 2019 PPMD Annual Conference,Conferences & Meetings 1:40:24 Our Voice Matters: Duchenne Town Hall Forum (PPMD 2019 Conference) 6 years ago 2019 PPMD Annual Conference,Conferences & Meetings «1…262728Page 28 of 28