Duchenne and the Heart (PPMD 2019 Conference) AGENDA 0:00 – Duchenne & the Heart Moderator: Abby Bronson 0:19 – Introduction & Overview – Linda Cripe, MD 16:07 – Outcome Measures for the Heart – Kan Hor, MD 37:01 – Second Generation Micro-Dystrophin – Dongsheng Duan, PhD 1:01:32 – Understanding Gene Therapy for the Heart – Lee Sweeney, PhD 1:22:15 – Cumberland Pharmaceuticals – Larry Markham, MD 1:37:00 – POLLING QUESTIONS 6 years ago 2019 PPMD Annual Conference,Conferences & Meetings You may also like 8:36 Here Is What I Hear — PPMD 2022 Annual Conference 3 years ago 2022 PPMD Annual Conference,Conferences & Meetings 39:20 The Future of Genetic Therapies — PPMD 2022 Annual Conference 3 years ago 2022 PPMD Annual Conference,Conferences & Meetings 1:30:40 Gene Therapy Approaches to Replace or Restore Dystrophin — PPMD 2022 Annual Conference 3 years ago 2022 PPMD Annual Conference,Conferences & Meetings 25:56 Gene Therapy Era: What We Know — PPMD 2022 Annual Conference 3 years ago 2022 PPMD Annual Conference,Conferences & Meetings 32:14 Duchenne Siblings Panel: What We Want You To Know — PPMD 2022 Annual Meeting 3 years ago 2022 PPMD Annual Conference,Conferences & Meetings 34:37 Parent Panel: Things I’d Like My Doctor To Know — PPMD 2022 Annual Conference 3 years ago 2022 PPMD Annual Conference,Conferences & Meetings 1:10:31 Brain and Behavior — PPMD 2022 Annual Conference 3 years ago 2022 PPMD Annual Conference,Conferences & Meetings 32:27 New Learnings on Natural History — PPMD 2022 Annual Conference 3 years ago 2022 PPMD Annual Conference,Conferences & Meetings «1…1011121314…28»Page 12 of 28