ACT DMD Update with PTC (February 2014) On February 5, 2014, Dr. Robert Spiegel, Chief Medical Officer at PTC Therapeutics, presented an update about PTC’s Phase 3 study of ataluren, now known as the Ataluren Confirmatory Trial in DMD (ACT DMD). 13 years ago Research & Clinical Trial Webinars,Webinars You may also like 56:15 An Update on Corticosteroids (October 2018) 8 years ago Care Webinars,Research & Clinical Trial Webinars,Webinars 44:29 Is Myostatin Still a Potential Therapeutic Target? (October 2018) 8 years ago Research & Clinical Trial Webinars,Webinars 1:00:51 Puberty and Duchenne (September 2018) 8 years ago Care Webinars,Webinars 1:09:04 HOPE-2 Duchenne Clinical Trial – Capricor (July 2018) 8 years ago Research & Clinical Trial Webinars,Webinars 1:01:35 Introducing PPMO – Sarepta Therapeutics (May 2018) 8 years ago Research & Clinical Trial Webinars,Webinars 50:18 Roche/Genentech Anti-Myostatin Adnectin RG6206 in Duchenne (May 2018) 8 years ago Research & Clinical Trial Webinars,Webinars 49:43 NS Pharma’s Exon 53 Skipping Program Update (April 2018) 9 years ago Research & Clinical Trial Webinars,Webinars 1:01:32 Gene Therapy: A Closer Look (March 2018) 9 years ago Research & Clinical Trial Webinars,Webinars gene therapy «1…1920212223…30»Page 21 of 30