October 1, 2019

Catabasis Completes Phase 3 PolarisDMD Trial Enrollment

Catabasis announced that the Phase 3 PolarisDMD trial for edasalonexent in Duchenne has completed enrollment and exceeded the target enrollment. PPMD is proud that The Duchenne Registry was able to play a role in helping…

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September 30, 2019

You can still join the fight to end Duchenne!

What an incredible Coach To Cure MD weekend! Our 12th anniversary season was our biggest to date with Werner Ladder joining the team as a national sponsor and Whataburger supporting us in the Southwest! With over 100…

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September 28, 2019

Today, we need YOU to Tackle Duchenne!

It’s GAMEDAY as we celebrate PPMD’s 12th Annual Coach To Cure MD, presented by Werner Ladder and we are so grateful to have teammates like you! Over 100 families and 450 universities are participating in the 12th…

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September 25, 2019

WATCH: Introduction to Gene Therapy [PPMD Gene Therapy Webinar Series]

For PPMD a pivotal aspect of care is education. Without the proper knowledge of what the potential benefits and risks are of an investigational product a family cannot make well informed decisions. As the landscape…

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September 25, 2019

Antisense Therapeutics Announces Positive Preliminary Results from ATL1102 for Duchenne Phase II Trial

Antisense Therapeutics has announced that a review of the preliminary data from the 6 patients who have completed their 24 weeks of dosing in the Phase II clinical trial of the company’s immunomodulatory therapy, ATL1102…

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September 25, 2019

Santhera Shares Fall 2019 Community Update

Santhera has shared a community update on the company’s Duchenne drug development programs and their partnership with ReveraGen. Click here to download.

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September 24, 2019

End Duchenne Tour Recap: Wilmington, Delaware

PPMD’s End Duchenne Tour made a stop in Wilmington, Delaware on September 14. We were joined by over 100 people, including 30 families, 20 healthcare professionals and researchers, 15 industry partners, and 5 members of…

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September 24, 2019

Coach To Cure MD Is This Weekend!

In honor of Coach To Cure MD, presented by Werner Ladder, on Saturday, September 28, we need YOU to join our team to help us #TackleDuchenne! Making forward progress is easy — just take a photo in…

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September 23, 2019

Italfarmaco Shares Fall 2019 Newsletter

Italfarmaco has shared the Fall 2019 issue of their newsletter, including updates on the Givinostat Development Program. Click here to download.

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September 18, 2019

Recap of PPMD’s Duchenne Platform Trial Community Meeting

On Monday September 9, PPMD along with I-ACT for Children and the Duchenne Regulatory Science Consortium (DRSC) held an open meeting inviting all stakeholders (patients, families, industry sponsors, and regulators) in Duchenne to learn and…

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