The Complexities of Duchenne (PPMD 2019 Conference)

AGENDA

1:40-3:15p – The Complexities of Duchenne
Moderator: Pat Furlong

• 1:40 – Duchenne: A Multisystem Disease – Stan Nelson, MD, PhD
• 2:00 – Variability: Modifiers to the Gene – Kevin Flanigan, MD
• 2:20 – Measuring Outcomes in the Face of Variability – Cliff Bechtold
• 2:40 – Challenges in Designing Trials – Craig McDonald, MD
• 3:00 – Q&A