August 15, 2022 /

Restoring Dystrophin via Exon Skipping Strategies — PPMD 2022 Annual Conference

Restoring Dystrophin via Exon Skipping Strategies

AOC 1044 – Mark Stahl, MD (Avidity Biosciences)
BMN 351 – Dave Jacoby MD, PhD (BioMarin Pharmaceutical Inc.)
DYNE-251 – Ash Dugar, PhD, MBA (Dyne Therapeutics)
ED051 – Michelle Mellion, MD (PepGen, Inc.)
ENTR-601-44 – Nerissa Kreher, MD, MBA (Entrada Therapeutics)
SRP-5051 – Teji Singh, MD (Sarepta Therapeutics)
WVE-N531 – Mike Panzara, MD, MPH (Wave Life Sciences)


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