Research Row: Exon-Skipping Strategies Sarepta Therapeutics ( SRP-5051) Dyne Therapeutics (DYNE-251) PepGen (EDO51) BioMarin Pharmaceutical (BMN351) Wave Life Sciences (WVE-N531) Entrada Therapeutics (ENTR-601-44) Avidity Biosciences (AOC 1044) NS Pharma (NS-089) 3 years ago 2023 PPMD Annual Conference,Conferences & Meetings You may also like 27:24 Our Stories Matter – Buddy Cassidy (PPMD 2019 Conference) 7 years ago 2019 PPMD Annual Conference,Conferences & Meetings 59:20 CRISPR: Future Strategies in Gene Therapy (PPMD 2019 Conference) 7 years ago 2019 PPMD Annual Conference,Conferences & Meetings gene therapy 33:56 Understanding Immunity (PPMD 2019 Conference) 7 years ago 2019 PPMD Annual Conference,Conferences & Meetings 1:28:49 Gene Correction (PPMD 2019 Conference) 7 years ago 2019 PPMD Annual Conference,Conferences & Meetings 1:40:24 Our Voice Matters: Duchenne Town Hall Forum (PPMD 2019 Conference) 7 years ago 2019 PPMD Annual Conference,Conferences & Meetings «1…262728Page 28 of 28