Research Row: Exon-Skipping Strategies Sarepta Therapeutics ( SRP-5051) Dyne Therapeutics (DYNE-251) PepGen (EDO51) BioMarin Pharmaceutical (BMN351) Wave Life Sciences (WVE-N531) Entrada Therapeutics (ENTR-601-44) Avidity Biosciences (AOC 1044) NS Pharma (NS-089) 2023 PPMD Annual Conference,Conferences & Meetings 2 years ago You may also like 45:00 Gene Therapy: Q&A 5 years ago Conferences & Meetings,In the Pipeline: Gene Therapy gene therapy 44:59 CINRG Expanded Duchenne Natural History Study (eDNHS) 5 years ago Conferences & Meetings,Foundations of Drug Development 37:11 Genetics & The Duchenne Registry 5 years ago Beginning the Duchenne Journey,Conferences & Meetings 24:30 Research & Clinical Trials 5 years ago Beginning the Duchenne Journey,Conferences & Meetings 4:10 PPMD Community: Getting Involved 5 years ago Beginning the Duchenne Journey,Conferences & Meetings 22:23 Advocacy & Community Engagement 5 years ago Beginning the Duchenne Journey,Conferences & Meetings 22:23 Navigating the Challenges of School 5 years ago Beginning the Duchenne Journey,Conferences & Meetings 24:00 Physical Therapy 5 years ago Beginning the Duchenne Journey,Conferences & Meetings «1…1819202122…28»Page 20 of 28