Research Row: Exon-Skipping Strategies Sarepta Therapeutics ( SRP-5051) Dyne Therapeutics (DYNE-251) PepGen (EDO51) BioMarin Pharmaceutical (BMN351) Wave Life Sciences (WVE-N531) Entrada Therapeutics (ENTR-601-44) Avidity Biosciences (AOC 1044) NS Pharma (NS-089) 3 years ago 2023 PPMD Annual Conference,Conferences & Meetings You may also like Approved Therapies & Sequential Therapy – PPMD 2025 Annual Conference 7 months ago 2025 PPMD Annual Conference,Conferences & Meetings How Do We Get to the Next Step in Research? The DCRN Explained – 2025 PPMD Annual Conference 7 months ago 2025 PPMD Annual Conference,Conferences & Meetings Dystrophin: The Missing Muscle Protein – 2025 PPMD Annual Conference 7 months ago 2025 PPMD Annual Conference,Conferences & Meetings Exercise: How Much is Too Much? – 2025 PPMD Annual Conference 7 months ago 2025 PPMD Annual Conference,Conferences & Meetings Navigating Behaviors: Strategies for Support & Success – 2025 PPMD Annual Conference 7 months ago 2025 PPMD Annual Conference,Conferences & Meetings Nurturing Mental Wellness in Everyday Life – 2025 PPMD Annual Conference 7 months ago 2025 PPMD Annual Conference,Conferences & Meetings Updates in Research & Care for Carriers – 2025 PPMD Annual Conference 7 months ago 2025 PPMD Annual Conference,Conferences & Meetings Therapies That Slow Progression – 2025 PPMD Annual Conference 7 months ago 2025 PPMD Annual Conference,Conferences & Meetings «1234…28»Page 2 of 28