July 17, 2023 /

Research Row Breakout Session: Exon Skipping Strategies – PPMD 2023 Annual Conference

Research Row: Exon-Skipping Strategies

  • Sarepta Therapeutics ( SRP-5051)
  • Dyne Therapeutics (DYNE-251)
  • PepGen (EDO51)
  • BioMarin Pharmaceutical (BMN351)
  • Wave Life Sciences (WVE-N531)
  • Entrada Therapeutics (ENTR-601-44)
  • Avidity Biosciences (AOC 1044)
  • NS Pharma (NS-089)

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