Research Row: Approved or on the Horizon Join us as we discuss Approved Therapies and those on the Horizon of approval. Santhera Pharmaceuticals (Vamorolone) Italfarmaco ( Givinostat) PTC Pharmaceuticals (Ataluren, Emflaza) Sarepta Therapeutics (Amondys45, Exondys 51, Vyondys53) NS Pharma (Viltepso) 3 years ago 2023 PPMD Annual Conference,Conferences & Meetings You may also like 48:44 Clinical Trials: A Panel Discussion on the Developmental Path – PPMD 2024 Annual Conference 2 years ago 2024 PPMD Annual Conference,Conferences & Meetings 21:30 Your Citizen Science at Work: How Pain Impacts Quality of Life – PPMD 2024 Annual Conference 2 years ago 2024 PPMD Annual Conference,Conferences & Meetings 55:02 Panel Conversation: Enhancing Social Experiences – PPMD 2024 Annual Conference 2 years ago 2024 PPMD Annual Conference,Conferences & Meetings 47:37 Research Row: PPMD Moving the Needle – PPMD 2024 Annual Conference 2 years ago 2024 PPMD Annual Conference,Conferences & Meetings 38:06 What Really Matters: A Town Hall on Life, Living, and Hope – PPMD 2024 Annual Conference 2 years ago 2024 PPMD Annual Conference,Conferences & Meetings 1:30:15 Newly Diagnosed & Duchenne 101 Discussions – PPMD 2024 Annual Conference 2 years ago 2024 PPMD Annual Conference,Conferences & Meetings 1:05:57 Reporting to You on PPMD Professional Meetings – PPMD 2024 Annual Conference 2 years ago 2024 PPMD Annual Conference,Conferences & Meetings 7:55 Next Steps and Closing Remarks – PPMD 2024 Annual Conference 2 years ago 2024 PPMD Annual Conference,Conferences & Meetings «1…56789…30»Page 7 of 30