Research Row: Approved or on the Horizon Join us as we discuss Approved Therapies and those on the Horizon of approval. Santhera Pharmaceuticals (Vamorolone) Italfarmaco ( Givinostat) PTC Pharmaceuticals (Ataluren, Emflaza) Sarepta Therapeutics (Amondys45, Exondys 51, Vyondys53) NS Pharma (Viltepso) 2 years ago 2023 PPMD Annual Conference,Conferences & Meetings You may also like 55:59 Decision Making around Steroids, Weight, and Nutrition – PPMD 2024 Annual Conference 1 year ago 2024 PPMD Annual Conference,Conferences & Meetings 47:28 Panel Conversation: The Little Things Matter – PPMD 2024 Annual Conference 1 year ago 2024 PPMD Annual Conference,Conferences & Meetings 36:59 OptimizeDMD: Moving the Dial in Endocrinology & Bone – PPMD 2024 Annual Conference 1 year ago 2024 PPMD Annual Conference,Conferences & Meetings 47:56 Research Row: Approaches to Alter Progression – PPMD 2024 Annual Conference 1 year ago 2024 PPMD Annual Conference,Conferences & Meetings 48:44 Clinical Trials: A Panel Discussion on the Developmental Path – PPMD 2024 Annual Conference 1 year ago 2024 PPMD Annual Conference,Conferences & Meetings 21:30 Your Citizen Science at Work: How Pain Impacts Quality of Life – PPMD 2024 Annual Conference 1 year ago 2024 PPMD Annual Conference,Conferences & Meetings 55:02 Panel Conversation: Enhancing Social Experiences – PPMD 2024 Annual Conference 1 year ago 2024 PPMD Annual Conference,Conferences & Meetings 47:37 Research Row: PPMD Moving the Needle – PPMD 2024 Annual Conference 1 year ago 2024 PPMD Annual Conference,Conferences & Meetings «1…34567…28»Page 5 of 28