Research Row: Approved or on the Horizon Join us as we discuss Approved Therapies and those on the Horizon of approval. Santhera Pharmaceuticals (Vamorolone) Italfarmaco ( Givinostat) PTC Pharmaceuticals (Ataluren, Emflaza) Sarepta Therapeutics (Amondys45, Exondys 51, Vyondys53) NS Pharma (Viltepso) 2 years ago 2023 PPMD Annual Conference,Conferences & Meetings You may also like 27:24 Our Stories Matter – Buddy Cassidy (PPMD 2019 Conference) 6 years ago 2019 PPMD Annual Conference,Conferences & Meetings 59:20 CRISPR: Future Strategies in Gene Therapy (PPMD 2019 Conference) 6 years ago 2019 PPMD Annual Conference,Conferences & Meetings gene therapy 33:56 Understanding Immunity (PPMD 2019 Conference) 6 years ago 2019 PPMD Annual Conference,Conferences & Meetings 1:28:49 Gene Correction (PPMD 2019 Conference) 6 years ago 2019 PPMD Annual Conference,Conferences & Meetings 1:40:24 Our Voice Matters: Duchenne Town Hall Forum (PPMD 2019 Conference) 6 years ago 2019 PPMD Annual Conference,Conferences & Meetings «1…262728Page 28 of 28